Assuming rare is required, the following results were found.

  • Cannabidiol Cuts Seizures in Another Rare Epilepsy

    or CBD, (Epidiolex) met its primary endpoint of reducing seizures in patients with tuberous sclerosis complex (TSC), a rare and severe form of childhood-onset epilepsy, a phase III pivotal trial showed here. Seizure frequency dropped from baseline by...

    https://mschristian.org/index.php/articles/2-uncategorised/9497-cannabidiol-cuts-seizures-in-another-rare-epilepsy
  • Chan Zuckerberg Initiative supports a patient-led movement to cure ALS

    to raising awareness of Amyotrophic lateral sclerosis (ALS) and empowering patients to lead the search for a cure. ALS is a rare and terminal neurological disease that robs people of their ability to move, speak, and eat in just a few years. The causes...

    https://mschristian.org/index.php/articles/2-uncategorised/8724-chan-zuckerberg-initiative-supports-a-patient-led-movement-to-cure-als
  • Rare Shrew-Borne Illness Tied to Fatal Encephalitis

    total number of reported cases of human Borna disease virus in southern Germany to at least 14, so it is still relatively rare in absolute numbers, but it might be behind a larger proportion of unexplained severe to fatal encephalitis cases," Beer said...

    https://mschristian.org/index.php/articles/2-uncategorised/9716-rare-shrew-borne-illness-tied-to-fatal-encephalitis
  • FDA Greenlight's Viela Bio's Uplizna for Rare Neuroinflammatory Autoimmune Disorder - BioSpace

    the past year. We continue to remain highly committed to the development of additional safe and effective drugs for this rare and devastating disease.” The other approved treatment is Alexion Pharmaceuticals’ Soliris (eculizumab). Although Viela Bio has...

    https://mschristian.org/index.php/articles/2-uncategorised/10857-fda-greenlight-s-viela-bio-s-uplizna-for-rare-neuroinflammatory-autoimmune-disorder-biospace
  • Cannabidiol Cuts Seizures in Another Rare Epilepsy

    or CBD, (Epidiolex) met its primary endpoint of reducing seizures in patients with tuberous sclerosis complex (TSC), a rare and severe form of childhood-onset epilepsy, a phase III pivotal trial showed here. Seizure frequency dropped from baseline by...

    https://mschristian.org/index.php/component/easyblog/cannabidiol-cuts-seizures-in-another-rare-epilepsy?Itemid=341
  • Newly discovered leukodystrophy in children: Potential cure

    sclerosis which interferes with this pathway. FULL STORY The Neurometabolic Diseases research team at IDIBELL and CIBER of Rare Diseases (CIBERER), led by ICREA Professor Aurora Pujol, has uncovered a novel disease of children affecting the brain white...

    https://mschristian.org/index.php/component/easyblog/newly-discovered-leukodystrophy-in-children-potential-cure?Itemid=341
  • FDA OKs First Drug for Pediatric Neurofibromas

    the nerve sheaths. "[I]n this critical time we want patients to know that the FDA remains committed to making patients with rare tumors and life threatening diseases, and their unique needs, a top priority," Richard Pazdur, MD, the FDA's top...

    https://mschristian.org/index.php/component/easyblog/fda-oks-first-drug-for-pediatric-neurofibromas?Itemid=341
  • Coronavirus Outbreak: Daily Updates

    Share on PinterestOver 2 million people in the U.S. have had COVID-19. Getty Images California researchers say that a rare type of antibody may help them develop a vaccine for COVID-19. Researchers from the University of California San Francisco and...

    https://mschristian.org/index.php/articles/2-uncategorised/10909-coronavirus-outbreak-daily-updates
  • Coronavirus Outbreak: Daily Updates

    Share on PinterestOver 2 million people in the U.S. have had COVID-19. Getty Images California researchers say that a rare type of antibody may help them develop a vaccine for COVID-19. Researchers from the University of California San Francisco and...

    https://mschristian.org/index.php/component/easyblog/coronavirus-outbreak-daily-updates?Itemid=101
  • Yale researchers uncover potential treatment for lethal Wolfram Syndrome

    Henderson, B.Sc.Jul 16 2020 Yale pharmacology professor Barbara Ehrlich and her team have uncovered a mechanism driving a rare, lethal disease called Wolfram Syndrome and also a potential treatment. Their findings appear in the July 6 edition of...

    https://mschristian.org/index.php/articles/2-uncategorised/10961-yale-researchers-uncover-potential-treatment-for-lethal-wolfram-syndrome
  • Rare Shrew-Borne Illness Tied to Fatal Encephalitis

    total number of reported cases of human Borna disease virus in southern Germany to at least 14, so it is still relatively rare in absolute numbers, but it might be behind a larger proportion of unexplained severe to fatal encephalitis cases," Beer said...

    https://mschristian.org/index.php/component/easyblog/rare-shrew-borne-illness-tied-to-fatal-encephalitis?Itemid=341
  • FDA Greenlight's Viela Bio's Uplizna for Rare Neuroinflammatory Autoimmune Disorder - BioSpace

    the past year. We continue to remain highly committed to the development of additional safe and effective drugs for this rare and devastating disease.” The other approved treatment is Alexion Pharmaceuticals’ Soliris (eculizumab). Although Viela Bio has...

    https://mschristian.org/index.php/component/easyblog/fda-greenlight-s-viela-bio-s-uplizna-for-rare-neuroinflammatory-autoimmune-disorder-biospace?Itemid=101
  • Right as Rain: Invisible Illnesses - Chapelboro.com

    to specialists around the world. It’s an incredible community of people bound together to learn more and better manage this rare disease for patients and their caregivers. I am proud to be a part of that community. Neuroendocrine cancer is often...

    https://mschristian.org/index.php/component/easyblog/right-as-rain-invisible-illnesses-chapelboro-com?Itemid=341
  • Newly discovered leukodystrophy in children: Potential cure

    sclerosis which interferes with this pathway. FULL STORY The Neurometabolic Diseases research team at IDIBELL and CIBER of Rare Diseases (CIBERER), led by ICREA Professor Aurora Pujol, has uncovered a novel disease of children affecting the brain white...

    https://mschristian.org/index.php/articles/2-uncategorised/5007-newly-discovered-leukodystrophy-in-children-potential-cure
  • Severe type I interferonopathy and unrestrained interferon signaling due to a homozygous germline mutation in STAT2 - Science

    at 3 months of age. Mother’s pregnancy with patient II:4 had been complicated by influenza B at 23 weeks’ gestation. A rare homozygous missense variant of STAT2 (Arg148Trp) segregates with disease Whole-exome sequencing analysis of genomic DNA from the...

    https://mschristian.org/index.php/component/easyblog/severe-type-i-interferonopathy-and-unrestrained-interferon-signaling-due-to-a-homozygous-germline-mutation-in-stat2-science?Itemid=341
  • FDA OKs First Drug for Pediatric Neurofibromas

    the nerve sheaths. "[I]n this critical time we want patients to know that the FDA remains committed to making patients with rare tumors and life threatening diseases, and their unique needs, a top priority," Richard Pazdur, MD, the FDA's top...

    https://mschristian.org/index.php/articles/2-uncategorised/10544-fda-oks-first-drug-for-pediatric-neurofibromas
  • Severe type I interferonopathy and unrestrained interferon signaling due to a homozygous germline mutation in STAT2 - Science

    at 3 months of age. Mother’s pregnancy with patient II:4 had been complicated by influenza B at 23 weeks’ gestation. A rare homozygous missense variant of STAT2 (Arg148Trp) segregates with disease Whole-exome sequencing analysis of genomic DNA from the...

    https://mschristian.org/index.php/articles/2-uncategorised/9542-severe-type-i-interferonopathy-and-unrestrained-interferon-signaling-due-to-a-homozygous-germline-mutation-in-stat2-science
  • Yale researchers uncover potential treatment for lethal Wolfram Syndrome

    Henderson, B.Sc.Jul 16 2020 Yale pharmacology professor Barbara Ehrlich and her team have uncovered a mechanism driving a rare, lethal disease called Wolfram Syndrome and also a potential treatment. Their findings appear in the July 6 edition of...

    https://mschristian.org/index.php/component/easyblog/yale-researchers-uncover-potential-treatment-for-lethal-wolfram-syndrome?Itemid=101
  • Everything you need to know about syringomyelia

    Table of contents Syringomyelia is a rare disorder in which a fluid filled cyst forms in the spinal cord. Cerebrospinal fluid surrounds and protects the brain and spinal cord. Syringomyelia happens when this fluid collects within the spinal cord and...

    https://mschristian.org/index.php/articles/2-uncategorised/9001-everything-you-need-to-know-about-syringomyelia
  • Thailand Asked to Consider Science in Vapor Regulation

    Scenes like this are rare in Thailand. This vaper in Koh Samui, Thailand could face fines or even jail. (Timothy S. Donahue) A consumer advocacy group wants the government of Thailand to consider science as basis for ending e-cigarette ban. The group...

    https://mschristian.org/index.php/articles/2-uncategorised/10905-thailand-asked-to-consider-science-in-vapor-regulation

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